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Publication
RNAi-Based Degradation of C9ORF72 Variants as a Potential Therapy for ALS
Gilbert, James
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Authors
Gilbert, James
UMass Chan Affiliations
RNA Therapeutics Institute
Keywords
ALS
Neuroscience
Oligonucleotide Therapeutics
C9ORF72
RNAi
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Morningside GSBS Dissertations and Theses
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https://hdl.handle.net/20.500.14038/51458
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